Health on MSN1y
What Is Beta Thalassemia?
Beta thalassemia is a blood disorder that affects the production of hemoglobin. Hemoglobin is the iron-rich protein in your ...
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Managing Non-Transfusion-Dependent Thalassemia Presents Challenges
Non-transfusion-dependent thalassemia encompasses three clinically distinct forms -- beta-thalassaemia intermedia, hemoglobin E/beta-thalassaemia (mild and moderate forms), and al ...
MedPage Today4d
Gene Therapy May Be a Game Changer for Transfusion-Dependent Thalassemia
The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...
pharmaphorum2y
Commercialization of novel gene-editing technology in beta-thalassemia
Beta-thalassemia is a rare blood disorder caused by a genetic defect in hemoglobin. Several manufacturers are developing novel treatments for the disease, including Vertex, which has partnered ...
2minutemedicine.com6d
Beti-cel gene therapy achieves high rates of transfusion independence in severe β-thalassemia
There were no serious adverse events or treatment-related mortalities. Evidence Rating Level: 2 (Good) Study Rundown: Transfusion-dependent β-thalassemia (TDT) is a condition that results in iron ...