Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New ...

Scientists have discovered more than a dozen genes that regulate the production of fetal hemoglobin in people of African ...

Sickle Cell Disease is a complex and debilitating ... It is caused by a mutation in the HBB gene, which leads to the production of abnormal haemoglobin known as haemoglobin S.

A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life, with doctors declaring him ...

Zynext Ventures is investing in Illexcor Therapeutics to advance the clinical development of ILX002, its lead candidate for ...

Research from UAB published in the New England Journal of Medicine in February 2022 suggests a gene therapy called LentiGlobin could provide a drastic improvement in quality of life for people with ...

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...

The influential Institute for Clinical and Economic Review (ICER) in the US has issued draft guidance suggesting that new gene therapies for sickle cell disease (SCD) from Vertex Pharma and ...

But in December, Beauzile, 21, became the first person in New York State to be made symptom-free of sickle cell disease after undergoing Lyfgenia, a new type of gene therapy that uses stem cell ...

Twenty-one-year-old Sebastien Beauzile was all smiles as he was serenaded with “Happy Birthday” on what he calls his new birthday at Cohen Children’s Medical ...

(CNN) — The US Food and Drug Administration on Friday approved two gene-based treatments for sickle cell disease, including the first therapy that uses the gene-editing technique CRISPR ...