Modern medicine is one step closer to potentially curing sickle cell disease ... palindromic repeats," which are repetitive sequences of DNA. "The CRISPR technology [that is] being used with ...

When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters was with a 24-year-old patient whose sickle ... a DNA sequence in BCL11A ...

However, in sickle cell disease and beta thalassemia ... in part because other DNA sequences often accompany the new gene inserted into the genome. These carryovers should be scrutinized to ...

In the UK, approximately 17,500 people have sickle cell disease and 300 babies are born with the condition each year. It is a genetic disorder caused by inherited mutations in a person's DNA that ...

This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD ... certain genetic diseases by targeting and altering specific DNA sequences.

By Gina Kolata Gina Kolata has reported on gene therapy for nearly 30 years and on sickle cell disease since 2018 ... to snip patients’ DNA. For a small number of subjects in clinical trials ...

India has one of the highest prevalences of sickle cell disease in the world ... stem cells from the bone marrow, cutting both DNA strands at the precise location in the BCL11A gene, and infusing ...

Today is World Sickle Cell Disease Day. The international awareness day is observed annually to increase public knowledge and an understanding of sickle cell disease and the challenges experienced ...

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...