The primary goals of AI personalization were to improve onboarding, boost medication initiation and adherence, and enhance physician follow-up. AllazoHealth’s artificial intelligence (AI)-powered ...

Arrowhead Pharmaceuticals announced the first patient treated in Takeda’s phase 3 REDWOOD trial of fazirsiran (TAK-999/ARO-AAT) for patients with alpha-1 antitrypsin deficiency (AATD)-associated liver ...

Short bursts of beta and gamma power were strongly associated with LGS and have potential as a novel biomarker. Unsupervised time-frequency analysis of electroencephalography (EEG) recorded from ...

Dan Lier has light chain (AL) amyloidosis—the most common form of amyloidosis. Larry Luxner, senior correspondent for Rare Disease Advisor, interviews former college basketball player Dan Lier, a ...

Researchers observed that sC5b-9 levels were proportional to the annual relapse rate after 1 year of follow up. Patients with neuromyelitis optica spectrum disorder (NMOSD) and high sC5b-9 levels ...

Over 80% achieved a clinically meaningful improvement in at least one of the scales assessed. Treatment with risdiplam over 30 months led to overall clinically meaningful improvement in most adult ...

The prevalence of AATD in the offspring of parents with AATD in our study was 37%. A risk of pregnancy complications and adverse birth outcomes has been observed in mothers with alpha-1 antitrypsin ...

Castleman disease and IgG4-RD have overlapping disease manifestations that can complicate the diagnostic process. A male patient initially suspected of having immunoglobulin G4-related disease ...

Twelve months after ASCT, chronic hemolysis is ongoing, but the patient is now transfusion-free, and the lymphoma is in continuous remission. Performing autologous stem cell transplantation (ASCT) in ...

The relationship between RA and AAV—two autoimmune disorders—needs further exploration. Rheumatoid arthritis (RA) is found to often precede the diagnosis of antineutrophil cytoplasmic antibody ...

The median levels of serum neurofilament light chain (sNfL) were greater in patients with CIDP who were treatment-naive compared to those who were on maintenance therapy. The levels of serum ...

Patients with ANCA-positive interstitial lung disease (ILD) exhibited a high prevalence of fibrotic patterns and mortality largely driven by the ILD itself. In patients with interstitial lung disease ...