Early results from the phase 1 SANRECO trial suggest that divesiran is safe and well tolerated, and may reduce the need for phlebotomy in patients with polycythemia vera by increasing hepcidin levels ...

When Logan and Erin Dorsey would visit Children’s of Mississippi for sickle cell disease care, they would ask for extra ...

Quesnel's Cyndi Logan spent $10,000 last time she received treatment, now she's worried the cost will be higher for the next ...

Corestemchemon Inc. is planning to file a BLA for Neuronata-R (lenzumestrocel) by the end of 2025 to gain accelerated ...

How far would you go to save your child? For Mina Holland, her second baby became his sister’s saviour in the fight against a ...

Results for IRAKLIA show noninferiority for Sanofi's on-body delivery system for isatuximab, compared with IV administration.

Only a handful of stem cell therapies are currently approved by the F.D.A., mainly for treating blood cancer and immune ...

Researchers have identified an early postnatal window that allows gene transfer to circulating blood stem cells, advancing ...

The novel drug reduces the need for burdensome phlebotomy and also addresses fatigue, thereby improving quality of life for ...

In bone marrow aspiration, a slim, hollow needle with a syringe attached is inserted into the bone marrow through a large bone at the back of the hip known as the posterior iliac crest.

Aspiration means the doctor or nurse draws some liquid bone marrow up into a syringe. A bone marrow trephine biopsy means they remove a very thin 1 or 2cm long core of bone marrow in one piece. You ...