Medication costs are only a piece of the puzzle when clinicians think about health care access, explains Leigh Maria Ramos-Platt, MD.

Shoppers Foundation for Women's Healthtm is now accepting applications for its 2025 Community Grants program, with a plan to give away $1.5M to charitable organizations working to make care more ...

HC Bioscience is shutting down after conducting preclinical models for a transfer RNA (tRNA) asset designed to treat ...

“Health Minute” brings original health care and health policy reporting from the KFF Health News newsroom to the airwaves each week. (3/18) Here's today's health policy haiku: ...

The patient, whom Sarepta described as a young man and later told news outlets was 16 years old, suffered acute liver failure ...

One patient with Duchenne muscular dystrophy (DMD) has passed away following treatment with Sarepta Therapeutics’ gene therapy Elevidys, the biotech ...

The Company is currently analyzing the case and will update the prescribing information for Elevidys to note this development.

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

The interim data found one child in the Duchenne trial produced more than double the amount of the protein needed to maintain ...

The death of a young boy with Duchenne muscular dystrophy (DMD) who was treated with Pfizer’s experimental gene therapy in a phase 2 trial has prompted the company to pause dosing in another study.

The FDA has placed another clinical hold on a gene therapy for Duchenne muscular dystrophy developed by Solid Biosciences, pulverising its share price. The halt of the IGNITE DMD trial was ...