Sickle Cell Disease is a complex and debilitating ... It is caused by a mutation in the HBB gene, which leads to the production of abnormal haemoglobin known as haemoglobin S.

View Full Profile. Learn about our Editorial Policies. Today, the cause of sickle cell disease is well understood to be a point mutation in a hemoglobin gene called HBB that makes red blood cells grow ...

Sickle-cell anemia is due to a mutation in the gene encoding the β-subunit of hemoglobin (called HBB), which leads to an abnormal structure of the β-subunit protein chain and the sickle-cell ...

Zynext Ventures is investing in Illexcor Therapeutics to advance the clinical development of ILX002, its lead candidate for ...

A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life, with doctors declaring him ...

Sebastien Beauzile became the first person in NY to be made symptom-free after undergoing a new type of gene therapy.

Sickle cell anemia is the most common inherited blood disorder and affects roughly 100,000 people in the United States at a given time. It's caused by a mutation of the hemoglobin gene ...

The purpose of the study is to evaluate the safety and ability of the autologous stem cell transplant with gene-edited stem cells to treat your sickle cell disease. BEAM-101 is the investigational ...

Starting in his early teens, Deshawn "DJ" Chow wasn't sure he'd ever be able to live a normal life. Crushing pain episodes brought on by his sickle cell disease were getting progressively worse.

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...