In the UK, approximately 17,500 people have sickle cell disease and 300 babies are born with the condition each year. It is a genetic disorder caused by inherited mutations in a person's DNA that ...

When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters was with a 24-year-old patient whose sickle ... a DNA sequence in BCL11A ...

India has one of the highest prevalences of sickle cell disease in the world ... stem cells from the bone marrow, cutting both DNA strands at the precise location in the BCL11A gene, and infusing ...

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...

says “sickle cell disease has always led the cutting edge of science discovery, whether it’s understanding the regulation of [genetic] promoter sequences or understanding protein biochemistry ...