Alzheimer's disease is the most common cause of dementia and affects more than a tenth of Americans aged 65 and older. The ...

"Sickle cell disease is a devasting disorder that affects approximately 100,000 people in the U.S., leading to anemia, severe ...

Two groundbreaking biotechnology advances are fundamentally altering human health and food production in 2025, moving from ...

Beam Therapeutics (NASDAQ: BEAM) , a biotechnology firm pioneering precision genetic medicines via base editing, announced it will present updated da ...

The child will need to be monitored throughout his life, but researchers said the treatment’s success indicates that other ...

G ene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has been challenging.

BEAM-101 is an investigational genetically modified ex vivo cell therapy for ... at targeted genomic sequences, without making double-stranded breaks in the DNA. This has the potential to enable ...

Sickle cell disease (SCD) is a group of genetic disorders that result in red blood cells, which carry oxygen through the body, having an abnormal, sickle-like shape. This can result in anemia ...

This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD ... certain genetic diseases by targeting and altering specific DNA sequences.

This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD ... certain genetic diseases by targeting and altering specific DNA sequences.

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...

When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters was with a 24-year-old patient whose sickle ... a DNA sequence in BCL11A ...