The company anticipates submitting a biologics licence application for accelerated approval in the US in early 2026.

The antimalarial drug mefloquine could help treat genetic diseases such as cystic fibrosis, Duchenne muscular dystrophy, as ...

Hantavirus, which is rare, shot to public attention after a New Mexico medical examiner announced that Gene Hackman’s wife Betsy Arakawa had died after contracting the virus. The bodies of ...

Eteplirsen may delay cardiac deterioration in DMD patients by reducing the risk ... in patients with confirmed mutation of the dystrophin gene amenable to exon 51 skipping. 2 However, data on ...

DMD is caused by mutations in the DMD gene that result in the lack of dystrophin, a protein that protects muscle cells from damage during movements. That lack of dystrophin results in progressive ...

Dire wolf pups born using gene-edited ancient DNA CRISPR used to match dire wolf genes in grey wolf embryos Dallas firm Colossal leads species restoration breakthrough ...

Following the Hulu show’s premiere, it’s sparked questions about the location. The area itself is beautiful, and looks nothing like the grim, grey cities of Gilead we’ve come to know.

DMD is a devastating genetic condition that primarily affects boys. It causes relentless muscle breakdown, loss of mobility in early adolescence, and premature death. With no cure currently available, ...

Get Instant Summarized Text (Gist) Gene therapy for Duchenne muscular dystrophy (DMD) faces challenges as the immune system may hinder its effectiveness. A large-scale trial showed that the ...

raises serious concerns about the effectiveness of gene therapy for Duchenne muscular dystrophy (DMD), after the treatment failed to show significant benefit in a large-scale clinical trial.

An independent data monitoring committee (DMC) favors continuing dosing Elevidys (delandistrogene moxeparvovec-rokl) to people with Duchenne muscular dystrophy (DMD) in ongoing clinical trials, ...

Hantavirus, the disease that caused the death of Betsy Arakawa, actor Gene Hackman’s wife, has claimed the lives of three people in California. After Arakawa, 65, was found dead along with ...