After a research note raised potential safety concerns with Amgen's lead obesity candidate, the company defended its drug and ...

RFK Jr. wants Americans to eat healthier by fixing what he deems is a corrupt food ecosystem. But this flies in the face of ...

Mirum is also initiating the Phase 3 EXPAND study, a label expansion opportunity for LIVMARLI in additional settings of cholestatic pruritus. CHOLBAM is FDA-approved for the treatment of bile acid ...

Anthony Bergmann; Chief Financial Officer; Capricor Therapeutics Inc. Linda Marban; President, Chief Executive Officer, Director; Capricor Therapeutics Inc. Ted Tent ...

Brooke was only three years old when she first learned about desmoid tumors. “My mother had six or seven,” she recalls.

First-ever FDA approval for gene therapy directly administered to the brain - - Priority review voucher granted - - Broad label including children and ... increasing the AADC enzyme and restoring ...

2: Clean Taste and Clean Label As a 100% wholegrain flour made from barley ... 5: Fibre Friendly Beta-glucans are not digested by the human enzymes of the small intestine, but are completely fermented ...

With that, let's move on to an update on our development program starting with our complement franchise and narsoplimab, our first-in-class MASP-2 inhibitor, targeting the effector enzyme of the ...

PTC Therapeutics submitted the BLA for Kebilidi in March 2024. The approval is based on data from a single, open-label trial ...

The FDA has followed in the footsteps of its European counterparts and granted accelerated approval to PTC Therapeutics’ gene ...

This is the first gene therapy for AADC deficiency to receive US regulatory approval and the first that can be administered directly to the brain.

The manufacturers are using various technologies such as automated garbage pickups, enzyme-based food management systems ...