In human cells, only a small proportion of the information written in genes is used to produce proteins. How does the cell ...

Gene editing is already being used to treat a handful of rare genetic diseases; however, most therapies involve breaking or inactivating genes. Precisely fixing disease-causing mutations is far more ...

The exact cause of Alzheimer’s disease has long evaded scientists, but experts typically suggest there are likely several ...

Rocket Pharmaceuticals, Inc.'s innovative therapies show promise after FDA setbacks. With potential $1B+ markets, RCKT offers ...

Human genes that encode proteins often contain non-coding segments known as introns. Removing introns is crucial for the proper expression of genetic information. Understanding how our cells ...

Boehringer will leverage ExpressionEdits' Genetic Syntax Engine which generates optimized introns to increase protein expression.

One in 10 Americans live with a rare disease, which often lacks effective treatments. Such is the case for PIGA-CDG, an ultra ...

In a new JAMA Dermatology study, scientists at King's College London found that changes in two parts of the genome work ...

Over 1,000 genes may serve as possible treatment targets for individuals with kidney disease, according to a new study. By creating the most complete and detailed genetic 'map' of kidney function to ...

Launched in 2021, Dallas-based Colossal Biosciences Inc. aims to reintroduce extinct species, some of which date back to the ...

KAIST researchers have discovered a molecular switch that can revert cancer cells back to normal by capturing the critical ...