Health and Me on MSN12d
These Are The Five Rare Diseases You Did Not Know Existed
It is always good to know about diseases so you can read the signs your body is telling you. However, there exists many ...
pharmaphorum4d
Inozyme plans $75m IPO as it heads for clinic with rare bone diseases drug
as the firm gears up for clinical trials of its lead drug for rare bone diseases. Based in Boston, Massachusetts, the company plans to raise $75 million by offering 5 million shares at a price ...
The American Journal of Managed Care28d
5 Rare Diseases That Now Have Their First FDA-Approved Treatments
Several rare disease patient populations received their ... ARSA gene introduced via a lentiviral vector and engraft within bone marrow. Following a conditioning regimen of high-dose chemotherapy ...
Their flesh turns to bone, but a new treatment might help them
That is the predicament of patients with fibrodysplasia ossificans progressiva (FOP) or “Stone Man Syndrome”, a rare musculoskeletal condition where, after birth and progressively through life, ...
Indiatimes19d
Coimbatore woman fights rare bone disorder, goes global with her paper dolls
While battling a rare bone disease that kept her away from school and social life, she has crafted more than 4,500 unique paper dolls and now runs a successful enterprise - Queenbee Paper Crafts ...
WSAZ29d
German bone marrow donor helps Nebraska woman beat rare disease
but she beat her rare disease thanks to a stranger in Germany, who they say is now family. Regina is an aplastic anemia survivor thanks to Achim Krause, a banker from Germany who banked his bone ...
University of Sheffield7d
Professor Nick Bishop
Clinical research group focuses on the treatment of childhood bone fragility and rare bone diseases; basic science group on early life events and skeletal development, as well as the pathophysiology ...