Modern medicine is one step closer to potentially curing sickle cell disease ... palindromic repeats," which are repetitive sequences of DNA. "The CRISPR technology [that is] being used with ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

However, in sickle cell disease and beta thalassemia ... in part because other DNA sequences often accompany the new gene inserted into the genome. These carryovers should be scrutinized to ...

When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters was with a 24-year-old patient whose sickle ... a DNA sequence in BCL11A ...

The Pediatric Emergency Medicine and Pediatric Hematology/Oncology divisions at MUSC have joined forces to create and test an ...

This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD ... certain genetic diseases by targeting and altering specific DNA sequences.

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke therapies can be widely applied ...

India has one of the highest prevalences of sickle cell disease in the world ... stem cells from the bone marrow, cutting both DNA strands at the precise location in the BCL11A gene, and infusing ...

A Fayetteville teen is making history in North Carolina after undergoing a new gene therapy for sickle cell disease. Aaron Scott was diagnosed with sickle cell at birth. Sickle cell is a genetic ...

Today is World Sickle Cell Disease Day. The international awareness day is observed annually to increase public knowledge and an understanding of sickle cell disease and the challenges experienced ...

For the first time, doctors have treated an infant with a rare genetic disease with a gene-editing therapy tailored specifically to the mutation he carries. KJ Muldoon was diagnosed with ...

LOS ANGELES, Sept 28 (Reuters) - Student Zoe Davis, 20, was just weeks into her junior year when she landed back in the hospital with severe sickle cell pain earlier this month. She is doing what ...