By Gina Kolata Gina Kolata has reported on gene therapy for nearly 30 years and on sickle cell disease since 2018. A panel of experts said on Tuesday that a groundbreaking treatment for sickle ...

The treatment of sickle cell disease is on the cusp of a historic breakthrough, with makers of two gene-based treatments for the debilitating blood disorder hoping for regulatory approval this year.

The Food and Drug Administration on Friday approved two gene therapies to treat sickle cell disease, one of the which is the first CRISPR/Cas9-based treatment to win regulatory approval in the US.

A bipartisan bill aimed at fighting sickle disease was signed into law by President Donald Trump on Tuesday night. The Sickle Cell Disease and Other Heritable Blood Disorders Research ...