In patients with antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV), high levels of baseline blood urea nitrogen (BUN) are a risk factor for end-stage kidney disease (ESKD) and/or ...

The change in extracellular volume is the only predictor of adverse outcome in patients with ATTR-CM treated with tafamidis, a study found.

Age over 75 years was significantly associated with reduced survival and shorter time on treatment. Ibrutinib remains an effective therapy for chronic lymphocytic leukemia (CLL), but older patients ...

Therapies for Gaucher disease generally fall into 2 main categories: enzyme replacement therapy (ERT) and substrate reduction therapy (SRT). Neither ERT nor SRT effectively treats the neurological ...

A patient with upper eyelid and submandibular swelling was eventually diagnosed and treated for IgG4-related disease.

Sole reliance on AFP levels for identifying hepatocellular carcinoma (HCC) may be insufficient for rendering an accurate diagnosis.

Two phase 3 clinical trials are recruiting patients with CIDP to evaluate the efficacy of riliprubart treatment.

The ECIL committee updated its guidelines on antifungal prophylaxis for patients with hematologic malignancies, including MDS, ALL, and CLL.

Pruritus may be associated with a poorer prognosis in patients with myelofibrosis (MF) and other myeloproliferative neoplasms, a study found.

Bruce is an advocate for Pompe disease. Confined to a wheelchair with complete paralysis, and being told he would never walk again, set Bruce in literal motion to engage in a range of sports and ...

Proteomics profiling has identified circulating biomarkers and dysregulated signaling in 2 pathways in patients with transthyretin-mediated amyloid cardiomyopathy (ATTR-CM).

A 16-year-old boy with Duchenne muscular dystrophy died of acute liver failure several months after receiving delandistrogene moxeparvovec-rokl (Elevidys®).