A group of questionnaires called PROfuture can meaningfully measure a variety of symptoms of SMA that impact patients, a study reported.

As treatment for spinal muscular atrophy (SMA) has drastically improved over the last decade, so too have survival rates and the number of people with SMA living well into adulthood. | A new education ...

More Hong Kong patients suffering from spinal muscular atrophy (SMA) will be able to enjoy a government subsidy to control ...

The list recommending customs duty of 5% includes 74 drugs, while another suggesting full exemption has 69 drugs. A separate ...

Remini shared an emotional tribute to the 21-year-old she met while filming the "King of Queens" sitcom: "I want people to ...

Differences may set most people apart, but not in the case of Milly and Asher, two kids going through treatment at Mary Free ...

The court said Switzerland’s refusal to pay for Spinraza for a quadriplegic patient with spinal muscular atrophy did not ...

Proposed cuts to the National Institutes of Health and the National Science Foundation “would cause immense and largely ...

For people like 16-year-old Vivienne Liedtke, who was born with the physical disability spinal muscular atrophy, finding a ...

Evrysdi treatment is safe and effective at improving or stabilizing motor and lung function in adults with SMA for up to 2 ...

After a season of regulatory upheaval, obesity and rare genetic diseases will likely remain major themes for biopharma in ...

Brain imaging in MSA revealed that distinct cerebellar and medullary atrophy patterns were closely linked to cardiovascular ...