News

Scholar Rock Reports New Employee Inducement Grants Under Nasdaq Listing Rule 5635(c)(4)
Scholar Rock (NASDAQ: SRRK; the "Company"), a late-stage biopharmaceutical company focused on developing and commercializing ...
Gulf Today6h
Al Jalila Children’s Hospital crosses 100 treatments for Spinal Muscular Atrophy
Al Jalila Children’s Hospital, part of Dubai Health, and the only children’s hospital in the UAE, has completed over 100 ...
SMA News Today10h
New ASAH1 mutation found to cause rare SMA type in boy, 4
A new ASAH1 mutation linked to SMA with progressive myoclonic epilepsy was found in a young boy, offering insights for ...
The Pharma Letter11h
ICER flags concerns over Scholar Rock’s apitegromab and other SMA drugs
The Institute for Clinical and Economic Review (ICER) has cast doubt on the value of a new spinal muscular atrophy treatment ...
The National on MSN11h
Syrian girl receives life-saving treatment as Dubai Ruler covers Dh7 million cost
A young Syrian girl with spinal muscular atrophy received Dh7 million gene therapy paid for by Sheikh Mohammed bin Rashid, Vice President and Ruler of Dubai, on Friday at Dubai Health's Al Jalila ...
Khaleej Times13h
'We were heard': Father thanks Dubai Ruler for Dh7 million that saved child's life
The family, Syrian nationals residing in the UAE, had launched an emotional plea on social media to save their daughter who ...